Duchenne muscular dystrophy


Paediatric clinical trials

Over the last 10 years, there has been great interest in researching new potential therapies and treatments for DMD. Several clinical trials are currently ongoing to: 

  • Investigate the safety and/or the efficacy of new drugs
  • Try to correct the genetic cause of DMD 
  • Protect the muscles from becoming weaker
Child under physical exam. Wikipedia
Child under physical exam. Wikipedia


Care recommendations for the management of DMD were first published in 2010. An update, published in January 2018 is now available. They describe evidence and expert opinions for the best care boys with DMD should receive at their clinical centre. A Duchenne Guide for Families is also available, based on the care recommendations. It provides comprehensive information about the management of DMD to families. The Duchenne Guide for Families is an extensive document. It might be easier to read the parts that are relevant for your child, based on:

  • His current age
  • Stage of the condition
  • A specific issue you would like to have more information about.

DMD family guide link

Last modified
08 October 2019